Importance: Testosterone (T) treatment increases bone mineral density (BMD) in men, but its effects on bone microarchitecture, a determinant of fracture risk, are unknown.
Objective: To determine the effect of T treatment on bone microarchitecture using high resolution-peripheral quantitative computed tomography (HR-pQCT).
Methods: Testosterone for Bone (T4Bone) is a sub-study of the Testosterone for the Prevention of Diabetes Mellitus (T4DM), a 2-year randomised placebo-controlled multicentre trial of injectable T undecanoate (TU) in men aged >50 years at high risk of diabetes.
Interventions: TU or placebo injections 3-monthly over 2 years on the background of a lifestyle program.
Main outcomes: Primary endpoint was cortical volumetric BMD (vBMD) at the distal tibia in 177 men in one centre. Secondary endpoints including other HR-pQCT parameters and bone remodelling markers. Areal BMD (aBMD) was measured by dual energy X-ray absorptiometry (DXA) in 601 men in five centres. Using a linear mixed model for repeated measures, the treatment effects were defined as mean adjusted differences (MAD [95% CI] over 2 years between groups.
Results: Baseline age was 60.2years, BMI 35.4kg/m2 and total T 14.2nmol/L. At the tibia, T treatment increased cortical vBMD by 9.33mgHA/cm3 [3.96;14.71], p<0.001 or 3.1% [1.2;5.0], total vBMD by 4.16mgHA/cm3 [2.14;6.19], p<0.001 or 1.3% [0.6;1.9]). T treatment also increased cortical area and thickness but effects on trabecular architecture were minor. Results at the radius were similar. T treatment reduced CTX -48.1ng/L [-81.1;-15.1] p<0.001 and P1NP -6.8mg/L [-10.9;-2.7], p<0.001). T treatment increased aBMD at the lumbar spine (0.04g/cm2 [0.03;0.05], p<0.001 or 3.3% [2.7;3.9]), and the total hip (0.01g/cm2 [0.01;0.02], p<0.001 or 1.9% [1.2;2.7]). The treatment effect was not dependent on baseline T or oestradiol.
Conclusion: In men, T treatment for 2 years increased volumetric bone density, predominantly via effects on cortical bone. The implications for fracture risk reduction require further study.